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Acid SphingoMyelinase Deficiency
Philadelphia, Pennsylvania
Acid SphingoMyelinase Deficiency Clinical Trials in Philadelphia, Pennsylvania
1 recruiting
Philadelphia, Pennsylvania
Showing
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1
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Recruiting
A Real-world Long-term Safety and Immunogenicity Study of Olipudase Alfa Therapy in Pediatric Patients Less Than 2 Years of Age With Acid Sphingomyelinase Deficiency (ASMD)
Acid SphingoMyelinase Deficiency
Niemann-Pick Diseases
Sanofi
10 enrolled
5 locations
NCT06192576
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