Alpha 1-Antitrypsin Deficiency Clinical Trials in Charleston, South Carolina
3 recruitingCharleston, South Carolina
Showing 1–3 of 3 trials
Recruiting
Phase 1Phase 2
A Study to Evaluate the Safety and Efficacy of BEAM-302 in Adult Patients With Alpha-1 Antitrypsin Deficiency (AATD)
Alpha 1-Antitrypsin Deficiency
Beam Therapeutics Inc.106 enrolled11 locationsNCT06389877
Recruiting
Phase 1
Study of BMN 349 Single Dose in PiZZ and PiMZ/MASH Adult Participants
Alpha 1-Antitrypsin Deficiency
BioMarin Pharmaceutical12 enrolled8 locationsNCT06738017
Recruiting
Phase 1
A Study of KB408 for the Treatment of Alpha-1 Antitrypsin Deficiency
Alpha 1-Antitrypsin Deficiency
Krystal Biotech, Inc.15 enrolled3 locationsNCT06049082