Alpha 1-Antitrypsin Clinical Trials in Charleston, South Carolina
5 recruitingCharleston, South Carolina
Showing 1–5 of 5 trials
Recruiting
Phase 3
A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)
Alpha 1-Antitrypsin Deficiency
Grifols Therapeutics LLC40 enrolled19 locationsNCT07555483
Recruiting
Phase 1Phase 2
A Study of TSRA-196 in Adults With PiZZ Alpha-1 Antitrypsin Deficiency (AATD)
Alpha 1-antitrypsin Deficiency (AATD)
Tessera Therapeutics, Inc.72 enrolled3 locationsNCT07227207
Recruiting
Phase 1Phase 2
A Study to Evaluate the Safety and Efficacy of BEAM-302 in Adult Patients With Alpha-1 Antitrypsin Deficiency (AATD)
Alpha 1-Antitrypsin Deficiency
Beam Therapeutics Inc.106 enrolled11 locationsNCT06389877
Recruiting
Phase 1
Study of BMN 349 Single Dose in PiZZ and PiMZ/MASH Adult Participants
Alpha 1-Antitrypsin Deficiency
BioMarin Pharmaceutical12 enrolled8 locationsNCT06738017
Recruiting
Phase 1
A Study of KB408 for the Treatment of Alpha-1 Antitrypsin Deficiency
Alpha 1-Antitrypsin Deficiency
Krystal Biotech, Inc.15 enrolled3 locationsNCT06049082