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Congenital, Hereditary, and Neonatal Diseases and Abnormalities
Hillsborough, North Carolina
Congenital, Hereditary, and Neonatal Diseases and Abnormalities Clinical Trials in Hillsborough, North Carolina
1 recruiting
Hillsborough, North Carolina
Showing
1–1
of
1
trials
Recruiting
Phase 3
Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
Muscular Dystrophy, Duchenne
DMD
Neuromuscular Diseases (NMD)
+10 more
Dyne Therapeutics
90 enrolled
1 location
NCT07608432
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