Dravet Syndrome Clinical Trials in Boston, Massachusetts
2 recruitingBoston, Massachusetts
Showing 1–2 of 2 trials
Recruiting
Phase 1Phase 2
A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome
Dravet Syndrome
Encoded Therapeutics47 enrolled10 locationsNCT05419492
Recruiting
Phase 3
A Double-blind Study Evaluating the Efficacy, Safety, and Tolerability of Zorevunersen in Patients With Dravet Syndrome
Dravet Syndrome
Stoke Therapeutics, Inc170 enrolled61 locationsNCT06872125