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Ectonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency
Philadelphia, Pennsylvania
Ectonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency Clinical Trials in Philadelphia, Pennsylvania
1 recruiting
Philadelphia, Pennsylvania
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1
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Recruiting
PROPEL - A Prospective Observational Patient Registry to Evaluate ENPP1 and ABCC6 Deficiency
ATP-Binding Cassette Subfamily C Member 6 Deficiency
Ectonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency
Inozyme Pharma
1,000 enrolled
14 locations
NCT06302439
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