Gaucher Disease Clinical Trials in San Francisco, California
3 recruitingSan Francisco, California
Showing 1–3 of 3 trials
Recruiting
International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry
Gaucher DiseaseCerebroside Lipidosis SyndromeGlucocerebrosidase Deficiency Disease+1 more
Genzyme, a Sanofi Company12,000 enrolled318 locationsNCT00358943
Recruiting
Registry of Patients Diagnosed With Lysosomal Storage Diseases
Mucopolysaccharidosis IMucopolysaccharidosis IIMucopolysaccharidosis VI+5 more
University of California, San Francisco250 enrolled1 locationNCT05619900
Recruiting
Phase 1
PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
Pompe Disease (Infantile-Onset)MPS VIIMPS I+6 more
University of California, San Francisco10 enrolled1 locationNCT04532047