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Gene Therapy
Boston, Massachusetts
Gene Therapy Clinical Trials in Boston, Massachusetts
1 recruiting
Boston, Massachusetts
Showing
1–1
of
1
trials
Recruiting
Phase 1
Phase 2
Phase I/II Trial of Lentiviral Gene Transfer for SCID-X1 With Low Dose Targeted Busulfan Conditioning
Gene Therapy
Severe Combined Immunodeficiency, X-Linked
David Williams
12 enrolled
4 locations
NCT03311503
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