Glycogen Storage Disease Type I Clinical Trials in Durham, North Carolina
5 recruitingDurham, North Carolina
Showing 1–5 of 5 trials
Recruiting
GBE Deficiency (GSD IV and APBD) Natural History Study
Glycogen Storage Disease Type IVAdult Polyglucosan Body DiseaseGSD4+2 more
Duke University200 enrolled1 locationNCT02683512
Recruiting
Pompe Disease Registry Protocol
Pompe DiseaseGlycogen Storage Disease Type II
Genzyme, a Sanofi Company2,000 enrolled272 locationsNCT00231400
Recruiting
Glycogen Storage Disease Type Ia (GSDIa) Disease Monitoring Program
Glycogen Storage Disease Type Ia
Ultragenyx Pharmaceutical Inc140 enrolled19 locationsNCT06636383
Recruiting
Pompe Pregnancy Sub-Registry
Pompe Disease (Late-onset)Glycogen Storage Disease Type II (GSD-II)Glycogenesis 2 Acid Maltase Deficiency
Genzyme, a Sanofi Company20 enrolled35 locationsNCT00567073
Recruiting
Phase 3
A Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18
Glycogen Storage Disease Type II Infantile Onset
Amicus Therapeutics36 enrolled14 locationsNCT04808505