Glycogen Storage Disease Type I Clinical Trials in Orange, California
3 recruitingOrange, California
Showing 1–3 of 3 trials
Recruiting
Pompe Disease Registry Protocol
Pompe DiseaseGlycogen Storage Disease Type II
Genzyme, a Sanofi Company2,000 enrolled272 locationsNCT00231400
Recruiting
Glycogen Storage Disease Type Ia (GSDIa) Disease Monitoring Program
Glycogen Storage Disease Type Ia
Ultragenyx Pharmaceutical Inc140 enrolled19 locationsNCT06636383
Recruiting
Phase 1Phase 2
A Phase 1/2, Dose-Exploration Study to Evaluate the Safety and Efficacy of BEAM-301 in Patients With Glycogen Storage Disease Type Ia (GSDIa)
Glycogen Storage Disease Type Ia
Beam Therapeutics Inc.36 enrolled3 locationsNCT06735755