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GM1 Gangliosidosis
Porto Alegre, Rio Grande do Sul
GM1 Gangliosidosis Clinical Trials in Porto Alegre, Rio Grande do Sul
1 recruiting
Porto Alegre, Rio Grande do Sul, Brazil
Showing
1–1
of
1
trials
Recruiting
Phase 3
A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis
GM1 Gangliosidosis
GM2 Gangliosidosis
Niemann-Pick Type C Disease
Azafaros A.G.
147 enrolled
37 locations
NCT07054515
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