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GM2 Gangliosidosis
Dallas, Texas
GM2 Gangliosidosis Clinical Trials in Dallas, Texas
1 recruiting
Dallas, Texas
Showing
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1
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Recruiting
Phase 3
A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis
GM1 Gangliosidosis
GM2 Gangliosidosis
Niemann-Pick Type C Disease
Azafaros A.G.
147 enrolled
37 locations
NCT07054515
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