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Hemoglobinopathies
Düsseldorf
Hemoglobinopathies Clinical Trials in Düsseldorf
1 recruiting
Düsseldorf, Germany
Showing
1–1
of
1
trials
Recruiting
Phase 3
Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease
Beta-Thalassemia
Sickle Cell Disease
Hematologic Diseases
+4 more
Vertex Pharmaceuticals Incorporated
26 enrolled
6 locations
NCT05477563
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