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Homocystinuria Due to CBS Deficiency
Doha, Qatar
Homocystinuria Due to CBS Deficiency Clinical Trials in Doha, Qatar
1 recruiting
Doha, Qatar, Qatar
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Natural History Study of Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (ACAPPELLA)
Homocystinuria Due to CBS Deficiency
Travere Therapeutics, Inc.
150 enrolled
11 locations
NCT02998710
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