Malformation Clinical Trials in Boston, Massachusetts
8 recruitingBoston, Massachusetts
Showing 1–8 of 8 trials
Recruiting
Phase 2Phase 3
Alpelisib in Pediatric and Adult Patients With Lymphatic Malformations Associated With a PIK3CA Mutation.
Lymphatic Malformations
Novartis Pharmaceuticals232 enrolled56 locationsNCT05948943
Recruiting
Phase 2
A Phase 2 Study of Mutant-selective PI3Kα Inhibitor, RLY-2608, in Adults and Children With PIK3CA Related Overgrowth Spectrum and Malformations Driven by PIK3CA Mutation
PIK3CA MutationVascular MalformationsPIK3CA-Related Overgrowth Spectrum (PROS)+4 more
Relay Therapeutics, Inc.277 enrolled31 locationsNCT06789913
Recruiting
Lymphatic Anomalies Registry for the Assessment of Outcome Data
Lymphatic MalformationCLOVES SyndromeKlippel Trenaunay Syndrome+7 more
Boston Children's Hospital1,000 enrolled1 locationNCT02399527
Recruiting
Pulmonary Embolism and Right-to-Left Shunts
Pulmonary Embolism (PE)StrokePulmonary Arteriovenous Malformation+3 more
Tufts Medical Center256 enrolled1 locationNCT07519876
Recruiting
Comprehensive HHT Outcomes Registry of the United States (CHORUS)
Gastrointestinal BleedingTelangiectasiaArteriovenous Malformations+4 more
Cure HHT10,000 enrolled16 locationsNCT06259292
Recruiting
Identification of Biomarkers for Patients with Vascular Anomalies
Vascular AnomalyKlippel Trenaunay SyndromeKaposiform Hemangioendothelioma+4 more
Children's Hospital Medical Center, Cincinnati1,000 enrolled2 locationsNCT03001180
Recruiting
Not Applicable
Treatment of Brain AVMs (TOBAS) Study
Arteriovenous MalformationsAVMUnruptured Brain Arteriovenous Malformation+2 more
Centre hospitalier de l'Université de Montréal (CHUM)1,000 enrolled30 locationsNCT02098252
Recruiting
Human Epilepsy Genetics--Neuronal Migration Disorders Study
EpilepsyCognition DisorderBrain Malformation+1 more
Harvard University Faculty of Medicine3,500 enrolled1 locationNCT00041600