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Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome
Aurora, Colorado
Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome Clinical Trials in Aurora, Colorado
1 recruiting
Aurora, Colorado
Showing
1–1
of
1
trials
Recruiting
Phase 1
Phase 2
ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS)
Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome
Ionis Pharmaceuticals, Inc.
48 enrolled
11 locations
NCT06430385
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