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MPS II
Barcelona
MPS II Clinical Trials in Barcelona
1 recruiting
Barcelona, Spain
Showing
1–1
of
1
trials
Recruiting
Phase 2
Phase 3
Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH
Mucopolysaccharidosis III
MPS IIIA
Sanfilippo Syndrome
+1 more
Ultragenyx Pharmaceutical Inc
36 enrolled
5 locations
NCT02716246
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