Clinical
Trials
Finder
Conditions
Drugs
Locations
Institutions
Guides
Search Trials
Get Alerts
Search
Conditions
Drugs
Locations
Institutions
Guides
Search Trials
Get Alerts
Conditions
MPS II
Columbus, Ohio
MPS II Clinical Trials in Columbus, Ohio
1 recruiting
Columbus, Ohio
Showing
1–1
of
1
trials
Recruiting
Phase 2
Phase 3
Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH
Mucopolysaccharidosis III
MPS IIIA
Sanfilippo Syndrome
+1 more
Ultragenyx Pharmaceutical Inc
36 enrolled
5 locations
NCT02716246
Feedback