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MPS VI
San Francisco, California
MPS VI Clinical Trials in San Francisco, California
1 recruiting
San Francisco, California
Showing
1–1
of
1
trials
Recruiting
Phase 1
PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
Pompe Disease (Infantile-Onset)
MPS VII
MPS I
+6 more
University of California, San Francisco
10 enrolled
1 location
NCT04532047
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