Clinical
Trials
Finder
Conditions
Drugs
Locations
Institutions
Guides
Search Trials
Get Alerts
Search
Conditions
Drugs
Locations
Institutions
Guides
Search Trials
Get Alerts
Conditions
Mucopolysaccharidosis I
Barcelona
Mucopolysaccharidosis I Clinical Trials in Barcelona
1 recruiting
Barcelona, Spain
Showing
1–1
of
1
trials
Recruiting
Phase 2
Phase 3
Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH
Mucopolysaccharidosis III
MPS IIIA
Sanfilippo Syndrome
+1 more
Ultragenyx Pharmaceutical Inc
36 enrolled
5 locations
NCT02716246
Feedback