Mucopolysaccharidosis I Clinical Trials in Oakland, California
2 recruitingOakland, California
Showing 1–2 of 2 trials
Recruiting
Phase 1
ISP-001: Sleeping Beauty Transposon-Engineered B Cells for MPS I
Mucopolysaccharidosis IH/SMucopolysaccharidosis IS
Immusoft of CA, Inc.11 enrolled2 locationsNCT05682144
Recruiting
Phase 2Phase 3
A Study to Determine the Efficacy and Safety of Tividenofusp Alfa (DNL310) vs Idursulfase in Pediatric and Young Adult Participants With Neuronopathic (nMPS II) or Non-Neuronopathic Mucopolysaccharidosis Type II (nnMPS II)
Mucopolysaccharidosis II
Denali Therapeutics Inc.63 enrolled32 locationsNCT05371613