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Mucopolysaccharidosis II
Philadelphia, Pennsylvania
Mucopolysaccharidosis II Clinical Trials in Philadelphia, Pennsylvania
1 recruiting
Philadelphia, Pennsylvania
Showing
1–1
of
1
trials
Recruiting
Phase 2
Phase 3
A Study to Determine the Efficacy and Safety of Tividenofusp Alfa (DNL310) vs Idursulfase in Pediatric and Young Adult Participants With Neuronopathic (nMPS II) or Non-Neuronopathic Mucopolysaccharidosis Type II (nnMPS II)
Mucopolysaccharidosis II
Denali Therapeutics Inc.
63 enrolled
32 locations
NCT05371613
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