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Mucopolysaccharidosis Type II
Saint Petersburg
Mucopolysaccharidosis Type II Clinical Trials in Saint Petersburg
1 recruiting
Saint Petersburg, Russia
Showing
1–1
of
1
trials
Recruiting
Phase 2
Phase 3
A Multi-cohort Study of Safety, Efficacy, PK and PD of GNR-055 in Patients With Mucopolysaccharidosis Type II
Metabolic Diseases
Mucopolysaccharidosis Type II
AO GENERIUM
32 enrolled
5 locations
NCT05208281
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