Muscular Dystrophy Clinical Trials in Rochester, New York
7 recruitingRochester, New York
Showing 1–7 of 7 trials
Recruiting
Phase 1
A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)
Duchenne Muscular Dystrophy
Insmed Gene Therapy LLC12 enrolled10 locationsNCT06817382
Recruiting
Phase 3
A Study to Evaluate Del-brax (Also Referred to as AOC 1020) in Participants With FSHD
facioscapulohumeral muscular dystrophyFascioscapulohumeral Muscular DystrophyFacio-Scapulo-Humeral Dystrophy+14 more
Avidity Biosciences, Inc.200 enrolled46 locationsNCT07038200
Recruiting
The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Children With Duchenne Muscular Dystrophy
Duchenne Muscular Dystrophy (DMD)
University of Rochester105 enrolled1 locationNCT07092540
Recruiting
Observation Study in Patients Age 0-5 Years With LAMA2-related Congenital Muscular Dystrophy
LAMA2-MD (Merosin Deficient Congenital Muscular Dystrophy, MDC1A)
Nationwide Children's Hospital44 enrolled14 locationsNCT06503367
Recruiting
Phase 1
Clenbuterol to Target DUX4 in FSHD
Muscular Dystrophy, Facioscapulohumeral
Jeffrey Statland30 enrolled3 locationsNCT06721299
Recruiting
Motor Outcomes to Validate Evaluations in Pediatric FSHD (MOVE Peds)
Muscular Dystrophy, Facioscapulohumeral
University of Kansas Medical Center80 enrolled7 locationsNCT06847282
Recruiting
Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
facioscapulohumeral muscular dystrophyMyotonic DystrophyMuscular Dystrophy+6 more
University of Rochester3,000 enrolled1 locationNCT00082108