Neuronal Ceroid Lipofuscinosis Clinical Trials in Hamburg
2 recruitingHamburg, Germany
Showing 1–2 of 2 trials
Recruiting
Phase 1Phase 2
A First-in-Human, Open-Label, Dose-Escalation Study to Evaluate the Safety and Tolerability of Gene Therapy With TTX-381 for the Ocular Manifestations Associated With Neuronal Ceroid Lipofuscinosis Type 2 (CLN2) Disease
Neuronal Ceroid Lipofuscinosis Type 2
Tern Therapeutics, LLC16 enrolled2 locationsNCT05791864
Recruiting
Natural History and Longitudinal Clinical Assessments in NCL / Batten Disease, the International DEM-CHILD Database
Batten DiseaseNeuronal Ceroid LipofuscinosisCLN1 Disease+12 more
Universitätsklinikum Hamburg-Eppendorf500 enrolled1 locationNCT04613089