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Paroxysmal Nocturnal Hemoglobinuria, PNH
Toronto, Ontario
Paroxysmal Nocturnal Hemoglobinuria, PNH Clinical Trials in Toronto, Ontario
1 recruiting
Toronto, Ontario, Canada
Showing
1–1
of
1
trials
Recruiting
Phase 1
Phase 2
A First-in-Human Safety and Efficacy Study of ALN-CFB, a Small Interfering RNA (siRNA) Targeting Complement Factor B, in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria With Persistent Anemia on a C5 Inhibitor
Paroxysmal Nocturnal Hemoglobinuria, PNH
Persistent Anemia
Regeneron Pharmaceuticals
24 enrolled
7 locations
NCT07187401
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