Pelizaeus-Merzbacher Disease Clinical Trials in Salt Lake City, Utah
2 recruitingSalt Lake City, Utah
Showing 1–2 of 2 trials
Recruiting
Phase 1
Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)
Pelizaeus-Merzbacher Disease
Ionis Pharmaceuticals, Inc.24 enrolled7 locationsNCT06150716
Recruiting
The Myelin Disorders Biorepository Project
AdrenoleukodystrophyCockayne SyndromeRefsum Disease+63 more
Children's Hospital of Philadelphia12,000 enrolled23 locationsNCT03047369