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Phelan-McDermid Syndrome
Beijing, Beijing Municipality
Phelan-McDermid Syndrome Clinical Trials in Beijing, Beijing Municipality
1 recruiting
Beijing, Beijing Municipality, China
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RB001 Gene Therapy Study in Children With SHANK3-related Phelan McDermid Syndrome (PMS)
Phelan-McDermid Syndrome
SHANK3 Haploinsufficiency
Peking University First Hospital
8 enrolled
1 location
NCT07014020
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