Pompe Disease (Infantile-Onset) Clinical Trials in San Francisco, California
2 recruitingSan Francisco, California
Showing 1–2 of 2 trials
Recruiting
Registry of Patients Diagnosed With Lysosomal Storage Diseases
Mucopolysaccharidosis IMucopolysaccharidosis IIMucopolysaccharidosis VI+5 more
University of California, San Francisco250 enrolled1 locationNCT05619900
Recruiting
Phase 1
PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
Pompe Disease (Infantile-Onset)MPS VIIMPS I+6 more
University of California, San Francisco10 enrolled1 locationNCT04532047