Phase 1 Recessive Clinical Trials
3 recruitingPhase 1
What is a Phase 1 trial?
Phase 1 trials test a new treatment in a small group of people for the first time. The primary goal is to evaluate safety, determine a safe dosage range, and identify side effects. These studies typically enroll 20 to 80 participants.
Showing 1–3 of 3 trials
Recruiting
Phase 1Phase 2
Targeting Collagen VII Antibodies With IV IgG in Dystrophic Epidermolysis Bullosa
Recessive dystrophic epidermolysis bullosaEpidermolysis BullosaDystrophic Epidermolysis Bullosa+1 more
M. Peter Marinkovich8 enrolled1 locationNCT06834035
Recruiting
Phase 1
The ENERGY Study: Evaluation of Safety and Tolerability of INZ-701 in Infants With ENPP1 Deficiency or ABCC6 Deficiency
Pseudoxanthoma ElasticumEctonucleotide Pyrophosphatase/phosphodiesterase1 DeficiencyAutosomal Recessive Hypophosphatemic Rickets+2 more
Inozyme Pharma16 enrolled7 locationsNCT05734196
Recruiting
Phase 1Phase 2
GMEB-SASS: A Gene-Modified Skin Substitute for RDEB Treatment
Recessive dystrophic epidermolysis bullosaEpidermolysis Bullosa Dystrophica, RecessiveRDEB
CHU de Quebec-Universite Laval9 enrolled1 locationNCT07193134