Phase 2 RNA Clinical Trials
24 recruitingPhase 2
What is a Phase 2 trial?
Phase 2 trials evaluate whether a treatment works for a specific condition and further assess its safety. These studies typically enroll several hundred participants and provide preliminary data on effectiveness.
Showing 1–20 of 24 trials
Recruiting
Phase 2
Haplo-identical Transplantation for Severe Aplastic Anemia, Hypo-plastic MDS and PNH Using Peripheral Blood Stem Cells and Post-transplant Cyclophosphamide for GVHD Prophylaxis
Paroxysmal Nocturnal Hemoglobinuria, PNHSevere Aplastic Anemia (SAA)Hypo-Plastic Myelodysplastic Syndrome (MDS)
National Heart, Lung, and Blood Institute (NHLBI)56 enrolled1 locationNCT03520647
Recruiting
Phase 1Phase 2
Safety, Tolerability, PK and PD of ADX-038 in Healthy Participants and Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients
Paroxysmal Nocturnal Hemoglobinuria, PNH
ADARx Pharmaceuticals, Inc.50 enrolled4 locationsNCT05876312
Recruiting
Phase 2
MT2023-20: Hematopoietic Cell Transplant With Reduced Intensity Conditioning and Post-transplant Cyclophosphamide for Severe Aplastic Anemia and Other Forms of Acquired Bone Marrow Failure.
Severe Aplastic AnemiaAcquired Amegakaryocytic ThrombocytopeniaAcquired Pure Red Cell Aplasia+1 more
Masonic Cancer Center, University of Minnesota60 enrolled1 locationNCT06412497
Recruiting
Phase 2
A Study to Compare the Effectiveness and Safety of T1695 Versus Ciclosporin in Participants With Moderate to Severe Vernal Keratoconjunctivitis
Moderate to Severe Vernal Keratoconjunctivitis
Laboratoires Thea120 enrolled11 locationsNCT07169695
Recruiting
Phase 1Phase 2
Study of Safety and Efficacy of HS-10542 in Patients With Paroxysmal Nocturnal Hemoglobinuria
Paroxysmal nocturnal hemoglobinuria
Jiangsu Hansoh Pharmaceutical Co., Ltd.50 enrolled1 locationNCT07470762
Recruiting
Phase 2Phase 3
PRECISION-BP: Precision Chronopharamacotherapy Targeting NP-RAAS-BP Rhythm Axis
ObesityCardiovascular DiseasesHypertension+3 more
University of Alabama at Birmingham160 enrolled1 locationNCT04971720
Recruiting
Phase 1Phase 2
A First-in-Human Safety and Efficacy Study of ALN-CFB, a Small Interfering RNA (siRNA) Targeting Complement Factor B, in Adult Participants With Paroxysmal Nocturnal Hemoglobinuria With Persistent Anemia on a C5 Inhibitor
Paroxysmal Nocturnal Hemoglobinuria, PNHPersistent Anemia
Regeneron Pharmaceuticals24 enrolled7 locationsNCT07187401
Recruiting
Phase 1Phase 2
Study to Evaluate the Safety and Immunogenicity of a Lyophilized Herpes Zoster Virus mRNA Vaccine
Herpes ZostermRNA Vaccine
Sinovac Biotech Co., Ltd519 enrolled1 locationNCT07400003
Recruiting
Phase 2
Gilteritinib Plus VA Followed By Consolidation Chemotherapy in Newly Diagnosed FLT3-ITD+ AML
Acute Myeloid LeukemiaIntermediate Risk Acute Myeloid LeukemiaFLT3 Internal Tandem Duplication Positive+1 more
First Affiliated Hospital of Zhejiang University25 enrolled1 locationNCT07259707
Recruiting
Phase 2
Induction Chemotherapy Combined With Tislelizumab for Locally Advanced Squamous Cell Carcinoma of the External Auditory Canal
Squamous Cell Carcinoma of External Auditory CanalLocally Advanced Tumor
Eye & ENT Hospital of Fudan University50 enrolled1 locationNCT07370337
Recruiting
Phase 2
Dornase Alfa and Cisplatin in Refractory Germ Cell Cancer.
Refractory Germ Cell TumorsDornase Alfa
National Cancer Institute, Slovakia33 enrolled1 locationNCT07121322
Recruiting
Phase 2
A Study of Pegcetacoplan in Pediatric Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)
Paroxysmal Nocturnal Hemoglobinuria, PNHParoxysmal Hemoglobinuria
Apellis Pharmaceuticals, Inc.12 enrolled12 locationsNCT04901936
Recruiting
Phase 2
A Phase II Study Evaluating the Efficacy and Safety of XH-S003 Capsules in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)
PNH - Paroxysmal Nocturnal Hemoglobinuria
S-INFINITY Pharmaceuticals Co., Ltd24 enrolled1 locationNCT06978699
Recruiting
Phase 2Phase 3
Long-term Safety and Tolerability of MY008211A Tablets in Patients With Paroxysmal Nocturnal Hemoglobinuria
Paroxysmal Nocturnal Hemoglobinuria, PNH
Wuhan Createrna Science and Technology Co., Ltd120 enrolled1 locationNCT06933914
Recruiting
Phase 2
Long-term Safety and Tolerability of HSK39297 in Patients With Paroxysmal Nocturnal Hemoglobinuria
Paroxysmal nocturnal hemoglobinuria
Haisco Pharmaceutical Group Co., Ltd.47 enrolled1 locationNCT06745622
Recruiting
Phase 2
Oxygen As an Acute Treatment in Alternating Hemiplegia of Childhood
Alternating Hemiplegia of Childhood
Assistance Publique - Hôpitaux de Paris24 enrolled2 locationsNCT06248645
Recruiting
Phase 2
Early Versus Conventional Cessation of Hydrocortisone in Septic Shock
Muscle WeaknessSeptic ShockHyperglycemia+4 more
Mahidol University160 enrolled1 locationNCT05818826
Recruiting
Phase 2
Long-Term Safety, Tolerability and Efficacy of OMS906 in Paroxysmal Nocturnal Hemoglobinuria
Paroxysmal nocturnal hemoglobinuria
Omeros Corporation25 enrolled5 locationsNCT06298955
Completed
Phase 2
In vivo assessment of triple agent thermo-responsive otic gels in patients with acute otitis externa. Phase 2 trial.
Otitis Externa
University of Queensland30 enrolled1 locationACTRN12618001896268
Terminated
Phase 2
Low dose of oral corticosteroids in the treatment of painful acute otitis externa (swimmer's ear)
Acute otitis externa
James Cook University250 enrolled1 locationACTRN12615000059561