Clinical
Trials
Finder
Conditions
Drugs
Locations
Institutions
Guides
Search Trials
Get Alerts
Search
Conditions
Drugs
Locations
Institutions
Guides
Search Trials
Get Alerts
Conditions
Spinal Muscular Atrophy (SMA)
Philadelphia, Pennsylvania
Spinal Muscular Atrophy (SMA) Clinical Trials in Philadelphia, Pennsylvania
1 recruiting
Philadelphia, Pennsylvania
Showing
1–1
of
1
trials
Recruiting
Phase 2
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
Spinal Muscular Atrophy (SMA)
argenx
60 enrolled
17 locations
NCT07287982
Feedback