Spinal Muscular Atrophy Clinical Trials in Columbia, Missouri
4 recruitingColumbia, Missouri
Showing 1–4 of 4 trials
Recruiting
Phase 2
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
Spinal Muscular Atrophy (SMA)
argenx60 enrolled17 locationsNCT07287982
Recruiting
Not Applicable
Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
Myasthenia GravisAmyotrophic Lateral SclerosisNeuromuscular Diseases (NMD)+15 more
University of Missouri-Columbia50 enrolled1 locationNCT07478172
Recruiting
Phase 2
Safety and Efficacy of NMD670 in Ambulatory Adult Patients With Type 3 Spinal Muscular Atrophy
Spinal Muscular Atrophy
NMD Pharma A/S54 enrolled31 locationsNCT05794139
Recruiting
Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
Spinal Muscular Atrophy (SMA)
Novartis Pharmaceuticals700 enrolled99 locationsNCT04174157