Phase 2 Telangiectasia Clinical Trials
3 recruitingPhase 2
What is a Phase 2 trial?
Phase 2 trials evaluate whether a treatment works for a specific condition and further assess its safety. These studies typically enroll several hundred participants and provide preliminary data on effectiveness.
Showing 1–3 of 3 trials
Recruiting
Phase 1Phase 2
A Study to Evaluate ALN-6400 in Healthy Volunteers and Patients With Hereditary Hemorrhagic Telangiectasia (HHT)
Hereditary hemorrhagic telangiectasia
Alnylam Pharmaceuticals120 enrolled16 locationsNCT06659640
Recruiting
Phase 1Phase 2
Safety and Efficacy of Mutation-targeted Precision Genetic Therapy for Ataxia-Telangiectasia (A-T)
Ataxia-telangiectasia
Timothy Yu10 enrolled1 locationNCT07215416
Recruiting
Phase 2
Efficacy of Nintedanib for Treatment of Epistaxis in Hereditary Hemorrhagic Telangiectasia (HHT) Patients
Telangiectasia, Hereditary Hemorrhagic
Dr. Romain Lazor48 enrolled3 locationsNCT04976036