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Transfusion Dependent Beta-Thalassaemia
Boston, Massachusetts
Transfusion Dependent Beta-Thalassaemia Clinical Trials in Boston, Massachusetts
1 recruiting
Boston, Massachusetts
Showing
1–1
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1
trials
Recruiting
Phase 1
Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies
Beta-Thalassemia
Sickle Cell Disease
Sickle Cell Anemia (HbSS, or HbSβ-thalassemia0)
+1 more
Daniel Bauer
10 enrolled
1 location
NCT06647979
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