Urea Cycle Disorders Clinical Trials in Los Angeles, California
2 recruitingLos Angeles, California
Showing 1–2 of 2 trials
Recruiting
Phase 1Phase 2
An Open-label Study to Investigate ECUR-506 in Male Babies Less Than 9 Months of Age With Neonatal Onset OTC Deficiency
Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency DiseaseUrea Cycle Disorders, Inborn+1 more
iECURE, Inc.20 enrolled12 locationsNCT06255782
Recruiting
Longitudinal Study of Urea Cycle Disorders
Brain Diseases, Metabolic, InbornAmino Acid Metabolism, Inborn ErrorsUrea Cycle Disorders
Andrea Gropman1,500 enrolled15 locationsNCT00237315