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X-linked Myotubular Myopathy
Pittsburgh, Pennsylvania
X-linked Myotubular Myopathy Clinical Trials in Pittsburgh, Pennsylvania
1 recruiting
Pittsburgh, Pennsylvania
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Recruiting
A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition
X-linked Myotubular Myopathy
Astellas Gene Therapies
50 enrolled
6 locations
NCT06581146
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