X-Linked Clinical Trials in San Francisco, California
5 recruitingSan Francisco, California
Showing 1–5 of 5 trials
Recruiting
Phase 1Phase 2
Study of EN-374 Gene Therapy in Participants With X-Linked Chronic Granulomatous Disease
X-Linked Chronic Granulomatous Disease
Ensoma15 enrolled9 locationsNCT06876363
Recruiting
Phase 3
Study of Bitopertin in Participants With EPP or XLP (APOLLO)
Erythropoietic Protoporphyria (EPP)X-Linked Protoporphyria (XLP)
Disc Medicine, Inc150 enrolled28 locationsNCT06910358
Recruiting
Phase 1Phase 2
A First-in-human Study of KK8123 in Adults With X-linked Hypophosphatemia
X-linked Hypophosphatemia
Kyowa Kirin Co., Ltd.24 enrolled9 locationsNCT06525636
Recruiting
The Myelin Disorders Biorepository Project
AdrenoleukodystrophyCockayne SyndromeRefsum Disease+63 more
Children's Hospital of Philadelphia12,000 enrolled23 locationsNCT03047369
Recruiting
CNKSR2 Natural History Study
Developmental DysphasiaEpileptic Encephalopathy, Childhood-OnsetX-Linked Intellectual Disability
University of California, San Francisco15 enrolled1 locationNCT06500260