Gene therapy Clinical Trials
2 recruitingGenetic
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Showing 1–2 of 2 trials
Recruiting
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Phase I/II Clinical Trial Stem Cell Gene Therapy in RAG1-Deficient SCID
Severe Combined Immunodeficiency Due to RAG1 Deficiency
Leiden University Medical Center10 enrolled7 locationsNCT04797260
Recruiting
Growth and Development-related Outcomes in Children With Transfusion-dependent Beta-thalassemia After Gene Therapy
Institute of Hematology & Blood Diseases Hospital, China100 enrolled1 locationNCT05991336