Natural History Study Clinical Trials
3 recruitingOther
Showing 1–3 of 3 trials
Recruiting
Otoferlin Gene-mediated Hearing Loss Natural History Study
Sensorineural Hearing Loss, Bilateral
Akouos, Inc.150 enrolled10 locationsNCT05572073
Recruiting
Study of BEST1 Vitelliform Macular Dystrophy
Retinitis PigmentosaBest Vitelliform Macular Dystrophy
Columbia University52 enrolled3 locationsNCT05809635
Recruiting
A Natural History Study in Children With a Type II Collagen Disorder With Short Stature
SEDCHypochondrogenesisSemd, Strudwick Type+1 more
Innoskel60 enrolled2 locationsNCT05408715