Clinical Trials in Gordonville, Pennsylvania
2 recruiting
Showing 1–2 of 2 trials
Recruiting
Phase 2
A Study to Investigate the Pharmacokinetics and Safety of Risdiplam in Infants With Spinal Muscular Atrophy
Muscular Atrophy, Spinal
Hoffmann-La Roche10 enrolled13 locationsNCT05808764
Recruiting
WiTNNess - TNNT1 Myopathy Natural History Study
MyopathyTNNT1-associated MyopathyInfantile-onset Nemaline Rod Myopathy+9 more
Clinic for Special Children40 enrolled1 locationNCT06374719