RecruitingNCT00903110

Global Patient Registry to Monitor Long-term Safety and Effectiveness of Increlex® in Children and Adolescents With Severe Primary Insulin-like Growth Factor-1 Deficiency (SPIGFD).


Sponsor

Esteve Pharmaceuticals, S.A.

Enrollment

500 participants

Start Date

Dec 9, 2008

Study Type

OBSERVATIONAL

Conditions

Summary

The Increlex® Global Registry is a descriptive, multicenter, observational, prospective, open-ended, non interventional, post-authorisation surveillance registry. The main purpose of this global registry is to collect, analyse and report safety data during and up to at least 5 years after the end of treatment in children and adolescents receiving Increlex® therapy for SPIGFD according to the locally approved product information.


Eligibility

Min Age: 2 YearsMax Age: 18 Years

Inclusion Criteria2

  • For US : patients starting or planning to start or currently receiving treatment with Increlex® therapy for severe primary IGF-1 deficiency as defined by the US Increlex® prescribing information or for growth hormone (GH) gene deletion who have developed neutralizing antibodies to GH.For EU : patients starting or planning to start or currently receiving treatment with Increlex® therapy according to the locally approved product information.
  • Parents or legally authorized representatives if applicable must give signed informed consent before any registry-related activities are conducted. Assent from the subject should also be obtained as appropriate

Exclusion Criteria5

  • Subject currently participating in an Increlex® clinical trial
  • Subject currently participating in any clinical trial for growth retardation
  • Patient with any contraindication to Increlex® or any condition subject to special warning as per the locally approved label
  • For US patients, these include patients with hypersensitivity to the active substance or any of the excipients, patients with active or suspected neoplasia and patients with closed epiphyses.
  • For EU patients: these include patients with hypersensitivity to the active substance or any of the excipients, patients with active or suspected neoplasia or any condition or medical history which increases the risk of benign or malignant neoplasia and patients with closed epiphyses

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Interventions

DRUGIncrelex®

Increlex® (mecasermin \[rDNA origin\] injection), 10 mg/ml solution for injection, 40-120mcg/kg BID or 0,04 to 0,12 mg/kg BID, as prescribed by physician


Locations(58)

Children's Hospital of Orange County

Orange, California, United States

University of Miami Leonard M Miller

Miami, Florida, United States

University Of Miami Leonard M. Miller

Miami, Florida, United States

D&H National Research Centers

Miami, Florida, United States

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

UT Southwestern Medical Center

Dallas, Texas, United States

Children's Health Specialty Center West Plano

Plano, Texas, United States

Salzkammergut-Klinik Vöcklabruck

Vöcklabruck, Austria

Hôpital Amiens-Picardie

Amiens, France

Centre Hospitalier de Blois

Blois, France

Hôpital Jean Verdier

Bondy, France

Hôpital Femme Mère-Enfant

Bron, France

Hôpital Estaing

Clermont-Ferrand, France

Hôpital Timone Enfants

Marseille, France

Hôpital Arnaud de Villeneuve

Montpellier, France

GHR Mulhouse Sud-Alsace

Mulhouse, France

Pole medical Bel'Air

Mulhouse, France

CHU Lenval

Nice, France

Hôpital Necker Enfants Malades

Paris, France

Hôpital Kremlin Bicetre

Paris, France

Hôpital des Enfants

Toulouse, France

Hôpital de Cayenne

Cayenne, French Guiana

Universitätsklinikum Erlangen Kinder- und Jugendklinik

Erlangen, Germany

Universitätsklinikum Heidelberg Kinderheilkunde

Heidelberg, Germany

Universitätskliniken des Saarlandes Kinderklinik

Homburg, Germany

Klinikum der Otto von Guericke Universität

Magdeburg, Germany

Klinikum Oldenburg

Oldenburg, Germany

Diabetologia Pediatrica Azienda Ospedaliero-Universitaria

Ancona, Italy

Ospedale di Bolzano

Bolzano, Italy

Spedali Civili di Brescia

Brescia, Italy

Azienda ospedaliera universitaria Meyer

Florence, Italy

I.R.C.C.S. Giannina Gaslini

Genova, Italy

U.O. Pediatria e Neonatologia Ospedale di Macerata

Macerata, Italy

Azienda Ospedaliera Universitaria II

Naples, Italy

Azienda Ospedaliera-Universitaria di Parma

Parma, Italy

Azienda USL-IRCCS

Reggio Emilia, Italy

Ospedale Pediatrico Bambino Gesù

Roma, Italy

Hôpital Pierre Zobda Quitman

Fort-de-France, Martinique

Samodzielny Publiczny Dzieciecy Szpital Kliniczny

Bialystok, Poland

Uniwersyteckie Centrum Kliniczne

Gdansk, Poland

Uniwersytecki Szpital Dziecięcy w Lublinie

Lublin, Poland

Szpital kliniczny im. Karola Jonschnera

Poznan, Poland

Kliniczny Szpital Wojewódzki

Rzeszów, Poland

Pomeranian Medical University

Szczecin, Poland

Hospital Univ Vall d'Hebrón

Barcelona, Spain

Hospital Parc Taulí de Sabadell

Barcelona, Spain

Hospital Sant Joan de Déu

Barcelona, Spain

Hospital Univ. de Cruces

Bilbao, Spain

Hospital Universitari Sant Joan de Reus

Reus, Spain

Hospital Universitario y Politécnico La Fe

Valencia, Spain

Linköping University Hospital

Linköping, Sweden

Karolinska Universitetssjukhuset

Stockholm, Sweden

Royal Belfast Hospital for Sick Children

Belfast, United Kingdom

Birmingham Children's Hospital

Birmingham, United Kingdom

Leeds General Infirmary

Leeds, United Kingdom

The Royal London Hospital

London, United Kingdom

Great Ormond Street Hospital

London, United Kingdom

Royal Manchester Children's Hospital

Manchester, United Kingdom

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NCT00903110