RecruitingNCT01522183

Atypical Hemolytic-Uremic Syndrome (aHUS) Registry

An Observational, Non-Interventional, Multi-Center, Multi-National Study of Patients With Atypical Hemolytic-Uremic Syndrome (aHUS Registry)


Sponsor

Alexion Pharmaceuticals, Inc.

Enrollment

3,000 participants

Start Date

Mar 18, 2013

Study Type

OBSERVATIONAL

Conditions

Summary

Post-marketing safety data on patients treated and untreated with eculizumab or ravulizumab.


Eligibility

Inclusion Criteria4

  • Male or female patients of any age, including minors, who have been diagnosed with aHUS
  • Patients with or without an identified complement pathogenic variant or anti-complement factor antibody
  • Able to give written informed consent. Patient or patient's parent/legal guardian must be willing and able to given written informed consent and the patient (if minor) must be willing to give written informed assent \[if applicable as determined by the central Institutional Review Boards/Independent Ethics Committees (IRB/IEC)\].
  • ADAMTS13 > 5%, if performed.

Exclusion Criteria2

  • Hemolytic Uremic Syndrome (HUS) only due to Shiga Toxin producing Escherichia coli (STEC).
  • Unable to give written informed consent. Patient or patient's parent/legal guardian unable to give written informed consent. Patient (if minor) unable to give written informed assent (if applicable as determined by the central Institutional Review Boards/Independent Ethics Committees \[IRB/IEC\]).

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Locations(141)

Clinical Trial Site

Aurora, Colorado, United States

Clinical Trial Site

Washington D.C., District of Columbia, United States

Clinical Trial Site

Gainesville, Florida, United States

Clinical Trial Site

Atlanta, Georgia, United States

Clinical Trial Site

Chicago, Illinois, United States

Clinical Trial Site

Boston, Massachusetts, United States

Clinical Trial Site

St Louis, Missouri, United States

Clinical Trial Site

Winston-Salem, North Carolina, United States

Clinical Trial Site

Columbus, Ohio, United States

Clinical Trial Site 1

Westmead, New South Wales, Australia

Clinical Trial Site 2

Westmead, New South Wales, Australia

Clinical Trial Site

Cairns, Queensland, Australia

Clinical Trial Site

Herston, Queensland, Australia

Clinical Trial Site

Woolloongabba, Queensland, Australia

Clinical Trial Site

Adelaide, South Australia, Australia

Clinical Trial Site

Heidelberg, Victoria, Australia

Clinical Trial Site

Parkville, Victoria, Australia

Clinical Trial Site

Parkville, Victoria, Australia

Clinical Trial Site

Murdoch, Western Australia, Australia

Clinical Trial Site

Nedlands, Western Australia, Australia

Clinical Trial Site

Brussels, Belgium

Clinical Trial Site

Brussels, Belgium

Clinical Trial Site

Brussels, Belgium

Clinical Trial Site (Adult)

Edegem, Belgium

Clinical Trial Site (Pediatric)

Edegem, Belgium

Clinical Trial Site (pediatric)

Ghent, Belgium

Clinical Trial Site (Adult)

Leuven, Belgium

Clinical Trial Site (pediatric)

Leuven, Belgium

Clinical Trial Site (Adult)

Liège, Belgium

Clinical Trial Site (pediatric)

Liège, Belgium

Clinical Trial Site (adult)

Woluwe-Saint-Lambert, Belgium

Clinical Trial Site (Pediatric)

Woluwe-Saint-Lambert, Belgium

Clinical Trial Site

London, Ontario, Canada

Clinical Trial Site

Toronto, Ontario, Canada

Clinical Trial Site

Montreal, Quebec, Canada

Clinical Trial Site

Québec, Quebec, Canada

Clinical Trial Site

Odense, Denmark

Clinical Trial Site 1

Amiens, France

Clinical Trial Site 2

Amiens, France

Clinical Trial Site

Angers, France

Clinical Trial Site

Bayonne, France

Clinical Trial Site

Bordeaux, France

Clinical Trial Site

Brest, France

Clinical Trial Site

Bron, France

Clinical Trial Site

Caen, France

Clinical Trial Site

Chambéry, France

Clinical Trial Site

Clermont-Ferrand, France

Clinical Trial Site

Dijon, France

Clinical Trial Site

Grenoble, France

Clinical Trial Site

Le Kremlin-Bicêtre, France

Clinical Trial Site

Lille, France

Clinical Trial Site

Lille, France

Clinical Trial Site

Lyon, France

Clinical Trial Site

Marseille, France

Clinical Trial Site

Montpellier, France

Clinical Trial Site 1

Nancy, France

Clinical Trial Site

Nancy, France

Clinical Trial Site

Nantes, France

Clinical Trial Site 1

Nantes, France

Clinical Trial Site

Nice, France

Clinical Trial Site 2

Paris, France

Clinical Trial Site 4

Paris, France

Clinical Trial Site 1

Paris, France

Clinical Trial Site 5

Paris, France

Clinical Trial Site 3

Paris, France

Clinical Trial Site

Perpignan, France

Clinical Trial Site

Poitiers, France

Clinical Trial Site

Pontoise, France

Clinical Trial Site

Rennes, France

Clinical Trial Site

Rennes, France

Clinical Trial Site 1

Rouen, France

Clinical Trial Site 2

Rouen, France

Clinical Trial Site 1

Strasbourg, France

Clinical Trial Site 2

Strasbourg, France

Clinical Trial Site

Toulouse, France

Clinical Trial Site

Toulouse, France

Clinical Trial Site

Tours, France

Clinical Trial Site

Valenciennes, France

Clinical Trial Site

Essen, Germany

Clinical Trial Site 1

Hanover, Germany

Clinical Trial Site 2

Hanover, Germany

Clinical Trial Site

Heidelberg, Germany

Clinical Trial Site

Lübeck, Germany

Clinical Trial Site

Münster, Germany

Clinical Trial Site

Tübingen, Germany

Clinical Trial Site

Beersheba, Israel

Clinical Trial Site 1

Bari, Italy

Clinical Trial Site 2

Bari, Italy

Clinical Trial Site

Florence, Italy

Clinical Trial Site

Genova, Italy

Clinical Trial Site 1

Milan, Italy

Clinical Trial Site 2

Milan, Italy

Clinical Trial Site

Milan, Italy

Clinical Trial Site

Roma, Italy

Clinical Trial Site

Torino, Italy

Clinical Trial Site

Lodz, Poland

Clinical Trial Site

Lodz, Poland

Clinical Trial Site 1

Moscow, Russia

Clinical Trial Site 2

Moscow, Russia

Clinical Trial Site

Saint Petersburg, Russia

Clinical Trial Site

Dongan, Chungcheongnam-do, South Korea

Clinical Trial Site

Seoul, Dongnam-ro, South Korea

Clinical Trial Site

Anyang-si, Gyeonggi-do, South Korea

Clinical Trial Site

Goyang-si, Gyeonggi-do, South Korea

Clinical Trial Site

Daegu, Hyeonchung-ro, South Korea

Clinical Trial Site

Gwangju, Jebong Ro, South Korea

Clinical Trial Site

Daegu, South Korea

Clinical Trial Site 1

Gyeonggi-do, South Korea

Clinical Trial Site 2

Gyeonggi-do, South Korea

Clinical Trial Site

Jeju-do, South Korea

Clinical Trial Site

Jeollabuk-do, South Korea

Clinical Trial Site 2

Seoul, South Korea

Clinical Trial Site 3

Seoul, South Korea

Clinical Trial Site 5

Seoul, South Korea

Clinical Trial Site 6

Seoul, South Korea

Clinical Trial Site 7

Seoul, South Korea

Clinical Trial Site 4

Seoul, South Korea

Clinical Trial Site 1

Seoul, South Korea

Clinical Trial Site 1

Barcelona, Spain

Clinical Trial Site 2

Barcelona, Spain

Clinical Trial Site

Pamplona, Spain

Clinical Trial Site

Seville, Spain

Clinical Trial Site

Basel, Switzerland

Clinical Trial Site

Bern, Switzerland

Clinical Trial Site

Surich, Switzerland

Clinical Trial Site

Kaohsiung City, Taiwan

Clinical Trial Site

New Taipei City, Taiwan

Clinical Trial Site

Taichung, Taiwan

Clinical Trial Site

Taoyuan, Taiwan

Clinical Trial Site

Ankara, Turkey (Türkiye)

Clinical Trial Site

Istanbul, Turkey (Türkiye)

Clinical Trial Site

Kayseri, Turkey (Türkiye)

Clinical Trial Site

Cardiff, United Kingdom

Clinical Trial Site

Exeter, United Kingdom

Clinical Trial Site

London, United Kingdom

Clinical Trial Site

London, United Kingdom

Clinical Trial Site

London, United Kingdom

Clinical Trial Site

Manchester, United Kingdom

Clinical Trial Site

Newcastle, United Kingdom

Clinical Trial Site

Southampton, United Kingdom

Clinical Trial Site

Wales, United Kingdom

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