RecruitingPhase 2NCT01656603

Safety Study of Unlicensed IND Cord Blood Units Manufactured by the National Cord Blood Program for Unrelated Transplantation

A Multicenter Safety Study of Unlicensed, Investigational Cryopreserved Cord Blood Units Manufactured by the National Cord Blood Program and Provided for Unrelated Hematopoietic Stem Cell Transplantation of Pediatric and Adult Patients


Sponsor

New York Blood Center

Enrollment

9,999 participants

Start Date

Feb 1, 2012

Study Type

INTERVENTIONAL

Conditions

Summary

This study will evaluate the safety of infusion of the investigational cord blood units by carefully documenting all infusion-related problems.


Eligibility

Inclusion Criteria3

  • Diagnosis: Patients with disorders affecting the hematopoietic system that are inherited, acquired, or result from myeloablative treatment.
  • Patients: Patients of any age and either gender
  • Cord blood product manufactured by the NCBP (at least one, if the graft contains more than one units)

Exclusion Criteria4

  • Patients who are receiving licensed cord blood products (only)
  • Patients who are receiving unlicensed cord blood products from other banks (only)
  • Patients who are transplanted at non-US transplant centers
  • Patients who are receiving cord blood products that will be "manipulated" post-thaw (e.g., ex vivo expansion, incubation in vitro, etc.)

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Interventions

BIOLOGICALunlicensed CBU

infusion of unlicensed cord blood units


Locations(71)

Children's of Alabama

Birmingham, Alabama, United States

Phoenix Children's Hospital

Phoenix, Arizona, United States

Mayo Clinic Arizona

Phoenix, Arizona, United States

University of Arizona Medical Center

Tucson, Arizona, United States

City of Hope

Duarte, California, United States

UCSD Moores Cancer Center

La Jolla, California, United States

Cedars Sinai Medical Center

Los Angeles, California, United States

UCLA Healthcare

Los Angeles, California, United States

Rady Children's Hospital

San Diego, California, United States

Stanford Health Care

Stanford, California, United States

The Children's Hospital of Colorado

Aurora, Colorado, United States

University of Colorado Hospital

Aurora, Colorado, United States

Presbyterian / St. Luke's Medical Center

Denver, Colorado, United States

Alfred I. DuPont Hospital for Children

Wilmington, Delaware, United States

Children's National Medical Center

Washington D.C., District of Columbia, United States

Nemour's Children's Clinic and Hospital

Jacksonville, Florida, United States

University of Miami Health System Sylvester Comprehensive Cancer Center

Miami, Florida, United States

University of Miami/Jackson Memorial Hospital

Miami, Florida, United States

Florida Hospital, Florida Center for Cellular Therapy

Orlando, Florida, United States

All Children's Hospital, John Hopkins Medicine

St. Petersburg, Florida, United States

Northside Hosptal

Atlanta, Georgia, United States

Children's Healthcare of Atlanta

Atlanta, Georgia, United States

Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, United States

Northwestern Memorial Hospital

Chicago, Illinois, United States

Loyola University Medical Center

Maywood, Illinois, United States

Midwestern Regional Medical Center

Zion, Illinois, United States

Indiana University

Indianapolis, Indiana, United States

James Graham Brown Cancer Center

Louisville, Kentucky, United States

National Institutes of Health

Bethesda, Maryland, United States

Massachusetts General Hospital

Boston, Massachusetts, United States

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Dana Farber Cancer Instistute

Boston, Massachusetts, United States

Children's Hospital of Michigan

Detroit, Michigan, United States

Henry Ford Health System

Detroit, Michigan, United States

Helen DeVos Children's Hospital

Grand Rapids, Michigan, United States

Mayo Clinic Rochester

Rochester, Minnesota, United States

University of Mississippi Medical Center

Jackson, Mississippi, United States

Barnes-Jewish Hospital at University of Washington / Sireman Cancer Center

St Louis, Missouri, United States

St. Louis University Hospital

St Louis, Missouri, United States

The Nebraska Medical Center

Omaha, Nebraska, United States

Northwell Health - North Shore University Hospital

Lake Success, New York, United States

Cohen Children's Medical Center of NY

New Hyde Park, New York, United States

New York Presbyterian Hospital WCMC

New York, New York, United States

Mount Sinai Hospital

New York, New York, United States

Memorial Sloan-Kettering Cancer Center

New York, New York, United States

University of Rochester Medical Center

Rochester, New York, United States

Akron Children's Hospital

Akron, Ohio, United States

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Seidman Cancer Center

Cleveland, Ohio, United States

Cleveland Clinic Foundation

Cleveland, Ohio, United States

Nationwide Children's Hospital

Columbus, Ohio, United States

Arthur G. James Cancer Hospital

Columbus, Ohio, United States

Stephenson Oklahoma Cancer Center

Oklahoma City, Oklahoma, United States

Southwestern Regional Medical Center

Tulsa, Oklahoma, United States

Doernbecher Children's Hospital / Oregon Health & Science University

Portland, Oregon, United States

Penn State Health / Penn State Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

Abramson Cancer Center of the University of Pennsylvania Medical Center

Philadelphia, Pennsylvania, United States

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Children's Hopsital of Pittsburgh of UPMC

Pittsburgh, Pennsylvania, United States

Medical University of South Carolina

Charleston, South Carolina, United States

St Jude Children's Research Center

Memphis, Tennessee, United States

Children's Medical Center of Dallas

Dallas, Texas, United States

Cook Children's Medical Center

Fort Worth, Texas, United States

Texas Children's Cancer Center

Houston, Texas, United States

Methodist Hospital / Texas Transplant Institute

San Antonio, Texas, United States

University of Virginia

Charlottesville, Virginia, United States

Virginia Commonwealth University Massey Cancer Center

Richmond, Virginia, United States

Fred Hutchinson Cancer Research Center / Seattle Cancer Care Alliance

Seattle, Washington, United States

West Virginia University Hospitals Inc

Morgantown, West Virginia, United States

University of Wisconsin Hospital and Clinics

Madison, Wisconsin, United States

Children's Hospital of Wisconsin

Milwaukee, Wisconsin, United States

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NCT01656603