RecruitingPhase 2Phase 3NCT01949129

Allogeneic Stem Cell Transplantation for Children and Adolescents With Acute Lymphoblastic Leukaemia


Sponsor

St. Anna Kinderkrebsforschung

Enrollment

1,800 participants

Start Date

Apr 1, 2013

Study Type

INTERVENTIONAL

Conditions

Summary

The ALL SCTped 2012 FORUM is a multinational, multi-centre, controlled, prospective phase III study for the therapy and therapy optimisation for children and adolescents with ALL in complete morphological remission (CR, less than 5% bone marrow blasts, no blasts in cerebrospinal fluid, no other extramedullary leukemia), who have an indication for HSCT with a myeloablative conditioning regimen. The stratification of patients in first and following remissions according to the individual transplantation modalities rests upon an indication for allogeneic HSCT and the availability of a suitable donor within the individual transplantation groups.


Eligibility

Min Age: 1 MonthMax Age: 18 Years

Inclusion Criteria15

  • Patients with ALL (except for patients with B-ALL) who fulfil the following criteria:
  • age at diagnosis ≤ 18 years. Age at HSCT ≤ 21 years
  • indication for allogeneic HSCT
  • complete remission (CR) before HSCT
  • written consent of the parents (legal guardian) and, if necessary, the minor patient via "Informed Consent Form"
  • no pregnancy
  • no secondary malignancy
  • no previous HSCT
  • HSCT is performed in a study participating centre
  • Non Hodgkin-Lymphoma
  • the whole protocol or essential parts are declined either by patient himself/herself or the respective legal guardian
  • no consent is given for saving and propagation of anonymous medical data for study reasons
  • severe concomitant disease that does not allow treatment according to the protocol at the investigator's discretion (e.g. malformation syndromes, cardiac malformations, metabolic disorders)
  • Karnofsky / Lansky score \< 50%
  • subjects unwilling or unable to comply with the study procedures

Interventions

DRUGVP16

60 mg/kg BW,1 day in TBI/VP16 conditioning; 40 mg/kg BW in Bu/VP16/Cy conditioning

RADIATIONTBI

2 x 2Gy/day , 3 days (total 12Gy)

DRUGThiotepa

2x5 mg/kg BW, 1 day

DRUGTreosulfan

14g/m² BS, 3 days

DRUGFludarabine

30 mg/m² BS, 5 days

DRUGBusulfan

iV, dosage according therapeutic drug monitoring, 4 days

DRUGATG Thymoglobulin

MD: ATG Thymo: 2,5mg/kg BW/d 3 days.

DRUGCyclophosphamide

as part of conditioning 60 mg/kg BW 2 days or as GvHD Prophylaxis 50mg/kg BW/d 2 days with Mesna

DRUGGrafalon

MD: 15mg/kg BW/d 3 days MMD: 10mg/kg BW/d 3 days


Locations(119)

Hospital de Pediatria "Juan P. Garrahan" Combate de Los Pozos N°1800 CABA

Buenos Aires, Argentina

Hospital Sor Maria Ludovica, Department Hematology Stem Cell Transplant Unit

La Plata, Argentina

Children's Cancer Centre The Royal Children's Hospital

Melbourne, Australia

Princess Margaret Hospital for Children

Perth, Australia

Sydney Children's Hospital

Randwick, Australia

Lady Cilento Children's Hospital

South Brisbane, Australia

The Children's Hospital at Westmead Oncology Unit

Sydney, Australia

Universitätsklinik für Kinder- und Jugendheilkunde, Abt. f. Hämato-Onkologie

Graz, Austria

Universitätsklinik für Kinder- und Jugendheilkunde

Innsbruck, Austria

St. Anna Children's Hospital, Vienna, Austria

Vienna, Austria

Belarusian Research Center for Pediatric Oncology, Hematology and Immunology

Minsk, Belarus

Hôpital Universitaire des Enfants Reine Fabiola (HUDERF)

Brussels, Belgium

Cliniques Universitaires Saint-Luc (UCL) Hématologie et oncologie pédiatrique

Brussels, Belgium

University Hospital Gent Pediatrische hemato-oncologie

Ghent, Belgium

University Hospitals Leuven Kinderhemato-oncologie

Leuven, Belgium

Centre Hospitalier Universitaire de Liège Domaine Universitaire du Sart Tilman

Liège, Belgium

Alberta Children's Hospital Division of Pediatric Oncology

Calgary, Canada

Montreal Children's Hospital

Montral, Canada

CHU Sainte-Justine Hematology-Oncology Division

Montreal, Canada

Hospital for Sick Children University of Toronto Division of Haematology/Oncology

Toronto, Canada

BC Children's Hospital

Vancouver, Canada

CancerCare Manitoba/University of Manitoba

Winnipeg, Canada

Hospital Dr Luis Calvo Mackenna

Santiago, Chile

Department of Pediatrics, UHC Zagreb

Zagreb, Croatia

Department of Pediatric Hematology and Oncology Teaching Hospital Motol, 2nd Medical School, Charles University

Prague, Czechia

Paediatric Stem Cell Transplant and Immune Deficiency, Dept. for children and adolescents 4072, Rigshospitalet

Copenhagen, Denmark

Division of Hematology-Oncology and Stem Cell Transplantation, Hospital for Children and Adolescents, Univ. of Helsinki

Helsinki, Finland

CHU Bordeaux

Bordeaux, France

CHU Clermont-Ferrand

Clermont-Ferrand, France

CHU Grenoble - Clinique Universitaire de Pédiatrie, Hôpital Couple Enfant

Grenoble, France

CHRU Lille, Service d'Hématologie Pédiatrique

Lille, France

IHOP / Lyon, Service Hématologie et d'Oncologie pédiatrique

Lyon, France

Hopital la Timone Adulte

Marseille, France

Hopital Arnaud de Villeneuve

Montpellier, France

CHU Nancy - Hopital d'Enfants

Nancy, France

CHU Nantes, Service d'onco hémato pédiatrie

Nantes, France

Hôpital Robert Debré

Paris, France

CHU de Rennes, Serive d'Onco-Pédiatrie

Rennes, France

CHU de Rouen, Hopital des Enfants, Service d' Immuno-Hématologie Oncologie Pédiatrique

Rouen, France

CHU Strasbourg, Service d'hématologie et d'oncologie pédiatrique

Strasbourg, France

Uniklinik RWTH Aachen, Kinder- und Jugendmedizin

Aachen, Germany

Charité - Universitätsmedizin Berlin, Campus Virchow-Klinikum

Berlin, Germany

Universitätsklinikum Bonn, Abteilung für Pädiatrische Hämatologie und Onkologie

Bonn, Germany

Universitätsklinikum Düsseldorf, Klinik für Kinder-Onkologie, -Hämatologie und Klinische Immunologie

Düsseldorf, Germany

Universitätsklinikum Erlangen, Kinder- und Jugendklinik

Erlangen, Germany

Universitätsklinikum Essen, Klinik für Kinderheilkunde III

Essen, Germany

Klinikum der Johann Wolfgang Goethe-Universität, Klinik für Kinder- und Jugendmedizin (KKJM)

Frankfurt am Main, Germany

Universitätsklinikum Freiburg, Zentrum für Kinder- und Jugendmedizin

Freiburg im Breisgau, Germany

Universitätsklinikum Gießen, Zentrum für Kinder- und Jugendmedizin

Giessen, Germany

Universitätsmedizin Greifswald, Klinik und Poliklinik für Kinder- und Jugendmedizin

Greifswald, Germany

Universitätsklinikum Halle (Saale), Universitätsklinik und Poliklinik für Kinder- und Jugendmedizin

Halle, Germany

Universitätsklinikum Hamburg-Eppendorf, Klinik und Poliklinik für Pädiatrische Hämatologie und Onkologie

Hamburg, Germany

Medizinische Hochschule Hannover, Zentrum Kinderheilkunde und Jugendmedizin

Hanover, Germany

Universitätsklinikum Heidelberg, Zentrum für Kinder- und Jugendmedizin

Heidelberg, Germany

Universitätsklinikum Jena, Sektion für Stammzelltransplantation

Jena, Germany

UKSH - Universitätsklinikum Schleswig-Holstein, Klinik für Allgemeine Pädiatrie

Kiel, Germany

Universitätsmedizin Leipzig, Abteilung für Pädiatrische Onkologie, Hämatologie und Hämostaseologie

Leipzig, Germany

Klinikum der Universität München, Dr. von Haunersches Kinderspital

München, Germany

Städt. Krankenhaus München Schwabing, Universitätskinderklinik der TU München

München, Germany

Universitätsklinikum Münster, Klinik für Kinder- und Jugendmedizin

Münster, Germany

Universitätsklinikum Regensburg, Klinik und Poliklinik für Kinder- und Jugendmedizin

Regensburg, Germany

Universitätsklinik für Kinder- und Jugendmedizin Tübingen

Tübingen, Germany

Universitätsklinikum Ulm, Klinik für Kinder- und Jugendmedizin

Ulm, Germany

Universitäts-Kinderklinik Würzburg

Würzburg, Germany

Saint Sophia Children's Hospital BMT Unit

Athens, Greece

National Institute of Haematology and Infectious Disease, Hospital of Southern Pest, Paediatric Bone Marrow Transplantation Unit

Budapest, Hungary

Rambam Medical Center

Haifa, Israel

Schneider Children's Medical Center of Israel

Petah Tikva, Israel

Dana Children's Hospital

Tel Aviv, Israel

Azienda Ospedaliero-Universitaria Policlinico S. Orsola-Malpighi di Bologna

Bologna, Italy

Ospedale Mayer di Firenze SODc Tumori Pediatrici e TMO

Florence, Italy

Istituto Gaslini Genova Oncoematologia Pediatrica-

Genoa, Italy

A.O. San Gerardo di Monza Clinica Pediatrica

Monza, Italy

A.O.R.N. Santobono Pausilipon, Dipartimento di Oncoematologia

Napoli, Italy

Azienda Ospedaliera di Padova Oncoematologia Pediatrica

Padua, Italy

Fondazione IRCCS Policlinico San Matteo

Pavia, Italy

Azienda Ospedaliero Universitaria Pisana U.O. di Oncoematologia Pediatrica A.O.

Pisa, Italy

Ospedale Pediatrico Bambino Gesù, Sapienza, University of Rome

Rome, Italy

Ospedale Infantile Regina Margherita SC Oncoematologia e Centro Trapianti

Torino, Italy

University of Malaya, Department of Paediatrics

Kuala Lumpur, Malaysia

Instituto Nacional de Peditria

Mexico City, Mexico

Leiden University Medical Center Department of Pediatrics/BMT unit

Leiden, Netherlands

Princess Máxima Center for Pediatric Oncology

Utrecht, Netherlands

Starship Children's Hospital

Auckland, New Zealand

Oslo University Hospital Rikshospitalet

Oslo, Norway

University Hospital No.1, Collegium Medicum UMK, department of Paediatrics, Oncology, Hematology and Paediatric Transplantology

Bydgoszcz, Poland

University Children's Hospital in Krakow, Department of Transplantation

Krakow, Poland

Children's University Hospital, Dept. Pediatric Hematology, Oncology, and Transplantology

Lublin, Poland

Poznan University of Medical Sciences, Department of Pediatric Onology, Hematology & HSCT

Poznan, Poland

Cape of Hope, Wroclaw Medical University

Wroclaw, Poland

IInsitutul Clinic Fundeni, Sectia de Transplant Medular

Bucharest, Romania

University of Medicine and Pharmacy V. BABES, Emergency Children's Hospital LOUIS TURCANU, III. Clinic of Pediatrics , Department of Onco-hematology and Bone Marrow Transplantation

Timișoara, Romania

King Abdullah specialists children hospital

Riyadh, Saudi Arabia

University Children's Hospital

Bratislava, Slovakia

University childrens' hospital, UMCL

Ljubljana, Slovenia

Hospital Santa Creu i Sant Pau

Barcelona, Spain

Hospital Vall d'Hebron

Barcelona, Spain

Hospital Materno Infantil de Málaga

Málaga, Spain

Hospital Virgen de la Arrixaca

Murcia, Spain

Hospital Universitario Central de Asturias

Oviedo, Spain

Queen Silvia Children's Hospital, Department of Pediatric Oncology (Avdelnig 321-322)

Gothenburg, Sweden

Skane University Hospital, Dept. of Pediatrics, Section for Hematology and Oncology

Lund, Sweden

Karolinska University Hospital, Department of Pediatrics

Stockholm, Sweden

University Children's Hospital, Dept. of Women's & Children's Health Section for Pediatrics

Uppsala, Sweden

Universitäts-Kinderspital beider Basel (UKBB)

Basel, Switzerland

HUG Hôpitaux Universitaire de Genève

Geneva, Switzerland

Universitäts-Kinderspital Zurich

Zurich, Switzerland

Ankara University School of Medicine Pediatric Stem Cell Transplantation Unit

Ankara, Turkey (Türkiye)

Gazi University School of Medicine Pediatric Stem Cell Transplantation Unit

Ankara, Turkey (Türkiye)

Gülhane Training and Research Hospital

Ankara, Turkey (Türkiye)

Akdeniz University School of Medicine Pediatric Stem Cell Transplantation Unit

Antalya, Turkey (Türkiye)

Bahcesehir University School of Medicine Pediatric Stem Cell Transplantation Unit

Antalya, Turkey (Türkiye)

Acibadem University Atakent Hospital Pediatric Stem Cell Transplantation Unit

Istanbul, Turkey (Türkiye)

Bahcelievler Medicalpark Hospital Pediatric Stem Cell Transplantation Unit

Istanbul, Turkey (Türkiye)

Bahcesehir University School of Medicine Pediatric Stem Cell Transplantation Unit

Istanbul, Turkey (Türkiye)

Medipol Mega Üniversite Hastanesi

Istanbul, Turkey (Türkiye)

Dokuzeylul University School of Medicine Pediatric Stem Cell Transplantation Unit

Izmir, Turkey (Türkiye)

Ege University School of Medicine Pediatric Stem Cell Transplantation Unit

Izmir, Turkey (Türkiye)

Erciyes University School of Medicine Pediatric Stem Cell Transplantation Unit

Kayseri, Turkey (Türkiye)

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