RecruitingPhase 2NCT02559778

Pediatric Precision Laboratory Advanced Neuroblastoma Therapy

A Study Using Molecular Guided Therapy With Induction Chemotherapy Followed by a Randomized Controlled Trial of Standard Immunotherapy With or Without DFMO Followed by DFMO Maintenance for Subjects With Newly Diagnosed High-Risk Neuroblastoma


Sponsor

Giselle Sholler

Enrollment

500 participants

Start Date

Sep 1, 2015

Study Type

INTERVENTIONAL

Conditions

Summary

A prospective open label, multicenter study to evaluate the feasibility and acute toxicity of using molecularly guided therapy in combination with standard therapy followed by a Randomized Controlled Trial of standard immunotherapy with or without DFMO followed by DFMO maintenance for Subjects with Newly Diagnosed High-Risk Neuroblastoma.


Eligibility

Max Age: 22 Years

Plain Language Summary

Simplified for easier understanding

This study is testing a personalized treatment approach for children and young adults with high-risk neuroblastoma (a type of childhood cancer that grows from nerve cells), aiming to tailor treatment based on the tumor's specific biology and how the patient has responded to previous treatment. **You may be eligible if...** - You are 21 years of age or younger at the time of initial diagnosis - You have been diagnosed with high-risk neuroblastoma or ganglioneuroblastoma, confirmed by biopsy or bone marrow testing - Your cancer has either just been diagnosed or has relapsed or become resistant to treatment - Your heart, liver, and kidneys are functioning adequately - You have enough healthy stem cells stored for transplantation (or can collect them) - If you are capable of becoming pregnant, you have had a negative pregnancy test and agree to use contraception **You may NOT be eligible if...** - Your cancer has low-risk features and does not meet the specific high-risk criteria - You are breastfeeding and unwilling to stop - You are currently participating in another clinical trial using an investigational drug - You have a medical or mental health condition that would prevent you from following the study requirements Talk to your doctor to see if this trial is right for you.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DRUGCeritinib

One of the following drugs will be chosen for each subject based on molecular guided results: Ceritinib, dasatinib, sorafenib or vorinostat. This will be followed by consolidation, immunotherapy +/- DFMO, and then all subjects will receive DFMO for 2 years as maintenance.

DRUGdasatinib

One of the following drugs will be chosen for each subject based on molecular guided results: Ceritinib, dasatinib, sorafenib or vorinostat. This will be followed by consolidation, immunotherapy +/- DFMO, and then all subjects will receive DFMO for 2 years as maintenance.

DRUGsorafenib

One of the following drugs will be chosen for each subject based on molecular guided results: Ceritinib, dasatinib, sorafenib or vorinostat. This will be followed by consolidation, immunotherapy +/- DFMO, and then all subjects will receive DFMO for 2 years as maintenance.

DRUGvorinostat

One of the following drugs will be chosen for each subject based on molecular guided results: Ceritinib, dasatinib, sorafenib or vorinostat. This will be followed by consolidation, immunotherapy +/- DFMO, and then all subjects will receive DFMO for 2 years as maintenance.

DRUGDFMO

DFMO will be given to Arm B during immunotherapy and then for 2 years as maintenance to all subjects completing immunotherapy.


Locations(28)

University of Alabama/Children's of Alabama

Birmingham, Alabama, United States

Arkansas Children's Hospital

Little Rock, Arkansas, United States

UCSF Benioff Children's Hospital Oakland

Oakland, California, United States

Rady Children's Hospital

San Diego, California, United States

Connecticut Children's Hospital

Hartford, Connecticut, United States

Nicklaus Children's Miami

Miami, Florida, United States

Arnold Palmer Hospital for Children

Orlando, Florida, United States

St. Joseph's Children's Hospital

Tampa, Florida, United States

Augusta University Health

Augusta, Georgia, United States

Kapiolani Medical Center for Women and Children

Honolulu, Hawaii, United States

St. Lukes

Boise, Idaho, United States

Advocate Aurora Research Institute

Chicago, Illinois, United States

Norton Children's Research Institute/Affiliated with University of Louisville School of Medicine

Louisville, Kentucky, United States

Helen DeVos Children's Hospital

Grand Rapids, Michigan, United States

Children's Hospital and Clinics of Minnesota

Minneapolis, Minnesota, United States

Children's Mercy Hospitals and Clinics

Kansas City, Missouri, United States

Cardinal Glennon Children's Medical Center

St Louis, Missouri, United States

Hackensack University Medical Center

Hackensack, New Jersey, United States

Levine Children's Hospital

Charlotte, North Carolina, United States

Randall Children's Hospital

Portland, Oregon, United States

Penn State Milton S. Hershey Medical Center and Children's Hospital

Hershey, Pennsylvania, United States

Medical University of South Carolina

Charleston, South Carolina, United States

Dell Children's Blood and Cancer Center

Austin, Texas, United States

Children's Medical Center

Dallas, Texas, United States

Alberta Children's Hospital

Calgary, Alberta, Canada

CHU Sainte-Justine

Montreal, Quebec, Canada

CHUQ

Québec, Quebec, Canada

CIUSSS de l'Estrie-CHUS

Sherbrooke, Quebec, Canada

View Full Details on ClinicalTrials.gov

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NCT02559778


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