RecruitingNCT03190837
A Long-term Follow-up Study of Gaucher Disease
Sponsor
Duke University
Enrollment
200 participants
Start Date
Jun 12, 2017
Study Type
OBSERVATIONAL
Conditions
Summary
The study aims are to: a) identify the long-term natural history of Gaucher disease, b) evaluate long-term treatment efficacy of enzyme replacement therapy (ERT) and substrate reduction therapy (SRT), and c) identify potential long-term complications of this disorder. These aims will be accomplished through long-term record review of individuals with all three types of Gaucher disease.
Eligibility
Inclusion Criteria1
- Diagnosis of Gaucher Disease
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Locations(1)
View Full Details on ClinicalTrials.gov
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NCT03190837
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