Gaucherite - A Study to Stratify Gaucher Disease
Predictive Measures to Stratify Clinical Outcomes in Children and Adults With Gaucher Disease and Responses to Specific Therapies
Cambridge University Hospitals NHS Foundation Trust
250 participants
Jan 1, 2014
OBSERVATIONAL
Conditions
Summary
The purpose of this research is to review data already collected and to collect new data from adults and children in England with Gaucher Disease to determine clinical factors which predict severity and response to therapy of Gaucher disease especially in the areas of bone, cancer and brain conditions.
Eligibility
Plain Language Summary
Simplified for easier understanding
This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.
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Interventions
Observational study involves review of retrospective and prospective data of participants' medical history, pathology, imaging and health questionnaires.
Locations(8)
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NCT03240653