RecruitingPhase 2NCT03509961

The EndRAD Trial: Eliminating Total Body Irradiation (TBI) for NGS-MRD Negative Children, Adolescents, and Young Adults With B-ALL

A Phase II Pilot Trial to Estimate Survival After a Non-total Body Irradiation (TBI) Based Conditioning Regimen in Patients Diagnosed With B-acute Lymphoblastic Leukemia (ALL) Who Are Pre-allogeneic Hematopoietic Cell Transplantation (HCT) Next-generation-sequence (NGS) Minimal Residual Disease (MRD) Negative


Sponsor

Pediatric Transplantation & Cellular Therapy Consortium

Enrollment

95 participants

Start Date

Aug 29, 2018

Study Type

INTERVENTIONAL

Conditions

Summary

This study will evaluate the use of non- TBI (total body irradiation) conditioning for B-ALL patients with low risk of relapse as defined by absence of NGS-MRD (next generation sequencing minimal residual disease) before receiving a hematopoietic cell transplant (HCT). Patients diagnosed with B-ALL who are candidates for HCT will be screened by NGS-MRD on a test of bone marrow done before the HCT. Subjects who are pre-HCT NGS-MRD negative will be eligible to receive a non-TBI conditioning regimen as part of the treatment cohort of the study. Subjects who are pre-HCT NGS-MRD positive will be treated as per treating center standard and will be followed in an observational cohort (HCT center standard of care).


Eligibility

Min Age: 1 YearMax Age: 25 Years

Plain Language Summary

Simplified for easier understanding

This trial is studying whether children, teenagers, and young adults with a type of leukemia called B-cell ALL who test negative for remaining cancer cells before a stem cell transplant can safely skip total body radiation — replacing it with chemotherapy alone — to reduce long-term side effects. **You may be eligible if...** - You are between 1 and 25 years old - You have B-cell acute lymphoblastic leukemia (B-ALL) in first or second remission - A specialized test (called NGS-MRD) shows no detectable cancer cells before your transplant - You have not had a previous stem cell transplant - You are in good enough health to undergo the transplant procedure **You may NOT be eligible if...** - Your MRD test before transplant shows remaining cancer cells - You are under 1 year old (you may still be enrolled in an observational arm) - You have T-cell leukemia or another leukemia type - You have previously had a stem cell transplant - Your cancer is in third or later remission Talk to your doctor to see if this trial is right for you.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DIAGNOSTIC_TESTNGS-MRD

Next generation sequencing minimal residual disease (NGS-MRD) is a test that has increased sensitivity over multichannel flow cytometry to better identify risk of key outcomes after HCT. Patients that have a pre-HCT negative NGS-MRD results may be eligible to proceed to the treatment arm of the study that uses a non-TBI conditioning regimen.

DRUGMyeloablative allogeneic HCT with a non-TBI conditioning regimen

Myeloablative study regimen will consist of busulfan, fludarabine and thiotepa. day -7: Fludarabine and Busulfan day -6: Fludarabine and Busulfan day -5: Fludarabine and Busulfan day -4: Fludarabine and Busulfan day -3: Fludarabine day -2: Thiotepa day -1: Rest Day 0: Transplant


Locations(24)

Children's of Alabama/University of Alabama in Birmingham(UAB)

Birmingham, Alabama, United States

Phoenix Children's Hospital

Phoenix, Arizona, United States

City of Hope

Duarte, California, United States

Children's Hospital Los Angeles

Los Angeles, California, United States

UCLA Mattel Children's Hospital

Los Angeles, California, United States

UCSF Benioff Children's Hospital Oakland

Oakland, California, United States

UCSF

San Francisco, California, United States

Children's Hospital Colorado

Aurora, Colorado, United States

Yale University School of Medicine

New Haven, Connecticut, United States

Alfred I. duPont Hospital for Children - Nemours Deleware

Wilmington, Delaware, United States

University of Florida

Gainesville, Florida, United States

Nicklaus Children's Hospital

Miami, Florida, United States

Johns Hopkins All Children's Hospital

St. Petersburg, Florida, United States

Children's Healthcare of Atlanta

Atlanta, Georgia, United States

Riley Hospital for Children - Indiana University

Indianapolis, Indiana, United States

Floating Hospital for Children at Tufts Medical Center

Boston, Massachusetts, United States

Dana Faber Cancer Institute/ Boston Children's Hospital

Boston, Massachusetts, United States

Helen DeVos Children's Hospital at Spectrum Health

Grand Rapids, Michigan, United States

Children's Mercy Hospital

Kansas City, Missouri, United States

Hackensack University Medical Center

Hackensack, New Jersey, United States

Roswell Park Cancer Institute

Buffalo, New York, United States

Atrium Health - Levine Cancer Center

Charlotte, North Carolina, United States

The University of Texas M. D. Anderson Cancer Center

Houston, Texas, United States

Methodist Healthcare System

San Antonio, Texas, United States

View Full Details on ClinicalTrials.gov

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