RecruitingNCT03827694

Non-Invasive Diagnosis of Pediatric Pulmonary Invasive Mold Infections


Sponsor

Arkansas Children's Hospital Research Institute

Enrollment

400 participants

Start Date

Oct 30, 2018

Study Type

OBSERVATIONAL

Conditions

Summary

This study will establish a non-invasive diagnostic approach and evaluate clinical outcomes for children at high-risk for pulmonary invasive fungal infection (PIFI).


Eligibility

Min Age: 120 DaysMax Age: 21 Years

Inclusion Criteria5

  • Males or females age > 120 days and < 22 years at any participating site
  • Have at least one of the following conditions associated with a known high incidence of IFI: hematopoietic stem cell transplantation (HSCT), aplastic anemia, bone marrow failure, primary or acquired immune deficiency, or malignancy
  • New (last 96 hours) radiographic evidence of at least one of the following: at least one nodular lesion greater than or equal to 5 mm in size, a wedge-shaped and segmental or lobar consolidation, a cavitary lesion, a lesion with a halo sign, a lesion with a reverse halo sign, or a lesion with an air crescent sign
  • Prolonged neutropenia (absolute neutrophil count < 500 cells/µl for a period of ≥ 5 consecutive days) in 30 days prior to and including the day of qualifying chest MRI or CT scan date OR currently receiving systemic therapy for acute or chronic graft-versus-host disease (GVHD) OR presence of neutrophil dysfunction because of underlying acquired or primary immune deficiency (e.g. chronic granulomatous disease) on the date of the qualifying chest MRI or CT scan
  • Subject consent or parental/guardian permission (informed consent) and if appropriate, child assent

Exclusion Criteria2

  • Weight <3 kg, so as to not exceed 3 ml/kg in a single blood draw
  • Previous inclusion in this study

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Interventions

DIAGNOSTIC_TESTNon-Invasive Testing for PIFI

galactomannan assay, fungal PCRs, cell-free next-generation DNA/RNA sequencing, RNAseq


Locations(33)

Arkansas Children's Research Institute

Little Rock, Arkansas, United States

Rady Children's Hospital, UCSD

La Jolla, California, United States

Children's Hospital of Orange County

Orange, California, United States

Lucile Packard Children's Hospital, Stanford University

Palo Alto, California, United States

University of California San Francisco, Benioff Children's Hospital

San Francisco, California, United States

Yale University

New Haven, Connecticut, United States

Children's National Hospital

Washington D.C., District of Columbia, United States

All Children's Research Institute

St. Petersburg, Florida, United States

Emory University-Children's Healthcare of Atlanta (CHOA)

Atlanta, Georgia, United States

Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, United States

University of Chicago Medicine, Comer Children's

Chicago, Illinois, United States

Indiana University School of Medicine

Indianapolis, Indiana, United States

Boston Children's Hospital

Boston, Massachusetts, United States

University of Minnesota Medical School

Minneapolis, Minnesota, United States

Children's Minnesota

Saint Paul, Minnesota, United States

Children's Mercy

Kansas City, Missouri, United States

The Washington University

St Louis, Missouri, United States

Children's Omaha

Omaha, Nebraska, United States

Weil Cornell Medical College

New York, New York, United States

Duke University Medical Center

Durham, North Carolina, United States

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Cleveland Clinic

Cleveland, Ohio, United States

Nationwide Children's Hospital

Columbus, Ohio, United States

Oregon Health and Science University

Portland, Oregon, United States

The Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

St. Jude Children's Research Hospital

Memphis, Tennessee, United States

Monroe Carell Jr. Children's Hospital at Vanderbilt

Nashville, Tennessee, United States

Ascension Seton Medical Center

Austin, Texas, United States

University of Texas Southwest Medical Center (UTSW)

Dallas, Texas, United States

MD Anderson

Houston, Texas, United States

Seattle Children's Research Institute

Seattle, Washington, United States

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

The Hospital for Sick Children

Toronto, Ontario, Canada

View Full Details on ClinicalTrials.gov

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NCT03827694